StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.
Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is a big problem: size.
Kebilidi is the first approved gene therapy that can be directly administered to the brain. Its OK secures a priority review ...
Zacks Small Cap Research on MSN9h
INAB: Upcoming Presentations at SNO & ASHINAB READ THE FULL INAB RESEARCH REPORT IN8bio, Inc (NASDAQ:INAB) reported third quarter 2024 financial results and achievements on November 12th. Activity since the second quarter update was ...
Clinical development and trial testing of vesleteplirsen (SRP-5051) for Duchenne muscular dystrophy (DMD) was stopped, with ...
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